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Research

Research
July 6 was my birthday, which means business as usual. I like it that way -- the fewer ...
Research
The goal of the Rett Syndrome Research Trust (RSRT) is to advance the most promising curative ...
Research
Every question you have ever had about gene replacement for Rett Syndrome is asked and answered ...
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MECP2 reactivation is a cornerstone therapeutic strategy at RSRT. The fact that this strategy ...
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The Rett Syndrome Research Trust has awarded $1.1 million dollars to a new collaboration taking ...
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Rett Syndrome is considered a rare disease; yet rare diseases, as a whole, are not rare—they ...
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At the Rett Syndrome Research Trust, we work to drive the development of cures for Rett ...
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A key aspect of effective clinical trials is the ability to objectively and accurately measure ...
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We are aware of concerns about the adenovirus vector COVID-19 vaccine from Johnson & ...
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Dear families and supporters, We want to share with you the update below from Novartis Gene ...
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A cure for Rett Syndrome. You want it. I want it. More than anything. So how is the Rett ...
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Dear families and supporters, We are excited to share the statement below from AveXis/Novartis ...
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The pace of scientific advance is rapidly enabling development of treatments targeting the core ...
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In a new study, mouse #895, also known as Henry the 8th, outlived most other models of Rett ...
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One day, Michael Greenberg was pondering the many unanswered questions about how the MeCP2 ...
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Dear Fellow Families, The events of the past several months have magnified how small our world ...
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I have had the privilege of working with the Rett Syndrome Research Trust (RSRT) for the past ...
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As more and more therapeutic development programs advance from basic scientific research into ...
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As we all know gut issues are common in Rett Syndrome and are often difficult to manage. ...
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Since our previous blog post on the RSRT website, we have made significant progress toward ...
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“Go big or go home” is a phrase I often use when describing RSRT’s research philosophy. ...
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Our community has been anxiously awaiting news from AveXis/Novartis regarding the start of the ...
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Rett Syndrome, like many other neurological disorders, relies on the interpretation of symptoms ...
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I am a scientist at Scripps Research Institute in La Jolla, California working in the lab of ...