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Yesterday was a tough day. The termination of the Novartis Rett gene replacement program, ...
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During Novartis’s quarterly investor call this morning the company informed the public that ...
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There is a great deal of excitement and anticipation surrounding gene replacement therapy in ...
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September 24, 2021 Dear Rett Syndrome Community, During the September 22 educational event on ...
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On September 22, 2021, Taysha Gene Therapies hosted a virtual educational event on Rett ...
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Shape Therapeutics (ShapeTX) is one of the seven biopharmaceutical companies taking aim at the ...
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News announced by Taysha Gene Therapies late last month brings us one step closer to testing a ...
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July 6 was my birthday, which means business as usual. I like it that way -- the fewer ...
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The goal of the Rett Syndrome Research Trust (RSRT) is to advance the most promising curative ...
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Every question you have ever had about gene replacement for Rett Syndrome is asked and answered ...
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MECP2 reactivation is a cornerstone therapeutic strategy at RSRT. The fact that this strategy ...
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The Rett Syndrome Research Trust has awarded $1.1 million dollars to a new collaboration taking ...
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Rett Syndrome is considered a rare disease; yet rare diseases, as a whole, are not rare—they ...
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At the Rett Syndrome Research Trust, we work to drive the development of cures for Rett ...
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A key aspect of effective clinical trials is the ability to objectively and accurately measure ...
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We are aware of concerns about the adenovirus vector COVID-19 vaccine from Johnson & ...
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Dear families and supporters, We want to share with you the update below from Novartis Gene ...
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A cure for Rett Syndrome. You want it. I want it. More than anything. So how is the Rett ...
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Dear families and supporters, We are excited to share the statement below from AveXis/Novartis ...
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The pace of scientific advance is rapidly enabling development of treatments targeting the core ...
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In a new study, mouse #895, also known as Henry the 8th, outlived most other models of Rett ...
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One day, Michael Greenberg was pondering the many unanswered questions about how the MeCP2 ...
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Dear Fellow Families, The events of the past several months have magnified how small our world ...
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I have had the privilege of working with the Rett Syndrome Research Trust (RSRT) for the past ...