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Rett In The News
Rett Syndrome Research Trust
Rett Syndrome Global Registry
Rett In The News
News from Taysha That We are One Step Closer to Testing Gene Replacement for Rett
September 2, 2021
A Reason to Celebrate: Children with a Severe Neurological Disorder Improve After Gene Replacement
July 6 was my birthday, which means business as usual. I like it that way -- the fewer ...
July 29, 2021
CURE 360 Webinar Series: Biopharma Tool Kit for Rett Syndrome Development Programs
The goal of the Rett Syndrome Research Trust (RSRT) is to advance the most promising curative ...
July 10, 2021
Cure 360 Webinar Series: Gene Replacement for Rett Syndrome 101
Every question you have ever had about gene replacement for Rett Syndrome is asked and answered ...
June 30, 2021
Cure 360 Webinar Series: Developing an Epigenetic Therapeutic for MECP2 Reactivation
MECP2 reactivation is a cornerstone therapeutic strategy at RSRT. The fact that this strategy ...
June 9, 2021
New Collaboration Intensifies Effort to Cure Rett Syndrome by Reactivating MECP2
The Rett Syndrome Research Trust has awarded $1.1 million dollars to a new collaboration taking ...
June 6, 2021
In their own words - members of RSRT’s newly formed Translational Medicine Advisory Board share their reasons for optimism
Rett Syndrome is considered a rare disease; yet rare diseases, as a whole, are not rare—they ...
June 3, 2021
Seven New RSRT-Supported Therapeutics Make Their Way Towards Clinical Trials
At the Rett Syndrome Research Trust, we work to drive the development of cures for Rett ...
May 26, 2021
Webinar: Assessing Rett Symptoms with Cutting Edge Biosensors and “Invisible” Technology.
A key aspect of effective clinical trials is the ability to objectively and accurately measure ...
April 23, 2021
Taysha Gene Therapies Statement on Covid-19 Vaccines
We are aware of concerns about the adenovirus vector COVID-19 vaccine from Johnson & ...
March 27, 2021
Novartis OAV201 Update
Dear families and supporters, We want to share with you the update below from Novartis Gene ...
February 9, 2021
The Next Phase of Our Attack on Rett: CURE 360
A cure for Rett Syndrome. You want it. I want it. More than anything. So how is the Rett ...
September 9, 2020
AveXis/Novartis Statement on AVXS-201
Dear families and supporters, We are excited to share the statement below from AveXis/Novartis ...
August 21, 2020
Enhancing the Potential Impact of Gene Therapy
The pace of scientific advance is rapidly enabling development of treatments targeting the core ...
June 28, 2020
Mutations Fighting Mutations
In a new study, mouse #895, also known as Henry the 8th, outlived most other models of Rett ...
May 6, 2020
The Power of Three
One day, Michael Greenberg was pondering the many unanswered questions about how the MeCP2 ...
April 17, 2020
Rett Research in a Time of Crisis
Dear Fellow Families, The events of the past several months have magnified how small our world ...
April 2, 2020
The Launch of a New Partnership
I have had the privilege of working with the Rett Syndrome Research Trust (RSRT) for the past ...
February 25, 2020
Biomarkers - What are they and why do we need them?
As more and more therapeutic development programs advance from basic scientific research into ...
February 25, 2020
Can Food be Medicine?
As we all know gut issues are common in Rett Syndrome and are often difficult to manage. ...
January 28, 2020
New Insight Into How MeCP2 Regulates Transcription
Since our previous blog post on the RSRT website, we have made significant progress toward ...
January 13, 2020
“Go big or go home” is a phrase I often use when describing RSRT’s research philosophy. ...
November 30, 2019
AveXis/Novartis Release Statement on AVXS-201
Our community has been anxiously awaiting news from AveXis/Novartis regarding the start of the ...
August 22, 2019
Biosensors and the Future of Rett Therapeutics
Rett Syndrome, like many other neurological disorders, relies on the interpretation of symptoms ...
August 14, 2019
Harnessing Exosomes as a Therapeutic for Rett Syndrome
I am a scientist at Scripps Research Institute in La Jolla, California working in the lab of ...
August 10, 2019