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Rett In The News

Spectrum
Increasing expression of the gene that is faulty in Rett syndrome lowers repetitive behaviors in a mouse model of a different autism-linked condition called Pitt-Hopkins syndrome, a new unpublished study demonstrates.
Taysha Gene Therapies
Taysha Gene Therapies today announced that it has been granted orphan drug designation from the European Commission for TSHA-102, an AAV9-based gene replacement therapy in development for Rett syndrome. An orphan designation allows a pharmaceutical company to benefit from incentives such as ...
c&en
A new class of therapies based on transfer RNA could treat forms of cystic fibrosis, muscular dystrophy, genetic epilepsies, and more
Endpoints News
Two years after spinning out of CRISPR pioneer Prashant Mali’s lab, Shape Therapeutics has a lot more cash and a slightly new mission. They have lead programs in Rett syndrome and Parkinson’s.

Recent Articles

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There is a great deal of excitement and anticipation surrounding gene replacement therapy in ...
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If you’re a Rett caregiver or family member, you know how many medical professionals it can ...
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The goal of the Rett Syndrome Research Trust (RSRT) is to advance the most promising curative ...
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The Rett Syndrome Research Trust has awarded $1.1 million dollars to a new collaboration taking ...
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Rett Syndrome is considered a rare disease; yet rare diseases, as a whole, are not rare—they ...
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Every question you have ever had about gene replacement for Rett Syndrome is asked and answered ...