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Gene Therapy

Gene Therapy
Every question you have ever had about gene replacement for Rett Syndrome is asked and answered ...
Gene Therapy
We are aware of concerns about the adenovirus vector COVID-19 vaccine from Johnson & ...
Gene Therapy
I told my daughter, Eleanor, the news. I had just put her in bed for the night. Her arms had ...
Gene Therapy
Mutations in a single gene, MECP2, can be identified in the vast majority of individuals with ...
Gene Therapy
We are excited to report to the Rett Syndrome community and to everyone who cares about an ...
Gene Therapy
Gene therapy is the lead program of our three-year strategic plan, Roadmap to a Cure. This ...
Gene Therapy
We’ve tried to anticipate some of the questions that families will have about Roadmap to a ...
Gene Therapy
Last week RSRT posted on Facebook an article about a gene therapy treatment for “bubble boy ...
Gene Therapy
In mid November the members of our Gene Therapy Consortium met in Boston to share data, and ...
Rett Syndrome Research Trust
Faced with the complex problem of discovering the elusive function of the Rett protein, RSRT ...
Rett Syndrome Research Trust
Sometimes, new ideas come from the strangest of places; inspired by something that seems ...
Rett Syndrome Research Trust
At the end of every year the Simons Foundation announces its list of most notable papers from ...